{"id":4980,"date":"2025-02-13T01:08:13","date_gmt":"2025-02-13T01:08:13","guid":{"rendered":"https:\/\/airna.docksal.site\/science-platform\/"},"modified":"2025-09-04T16:47:03","modified_gmt":"2025-09-04T16:47:03","slug":"science-platform","status":"publish","type":"page","link":"https:\/\/airna.com\/de\/science-platform\/","title":{"rendered":"Wissenschaft und Plattform"},"content":{"rendered":"\n<div class=\"wp-block-cover alignfull\"><span aria-hidden=\"true\" class=\"wp-block-cover__background has-blue-dk-background-color has-background-dim-100 has-background-dim\"><\/span><div class=\"wp-block-cover__inner-container is-layout-constrained wp-block-cover-is-layout-constrained\">\n\t<div  class=\"section-heading  align-text-left align-content-top align wp-block-acf-section-heading\">\n\t\n\n\t\t<div class=\"acf-innerblocks-container\">\n\n<div class=\"wp-block-group is-layout-constrained wp-block-group-is-layout-constrained\">\n<div class=\"wp-block-group is-style-offset-left section-heading__heading is-layout-constrained wp-block-group-is-layout-constrained\">\n<h2 class=\"wp-block-heading eyebrow-preheading\">Neue Erkenntnisse zu Genmedikamenten umsetzen<\/h2>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h3 class=\"wp-block-heading has-h-2-font-size\">Wir steuern ein nat\u00fcrlich vorkommendes menschliches Protein pr\u00e4zise um, so dass es therapeutischen Nutzen entfaltet.<\/h3>\n<\/div>\n\n\n\n<div class=\"wp-block-group is-style-offset-right section-heading__content is-layout-constrained wp-block-group-is-layout-constrained\">\n<p>Unser K\u00f6rper verwendet auf nat\u00fcrliche Weise das Protein Adenosinedeaminase, das auf die RNA wirkt (protein <strong>a<\/strong>denosine <strong>d<\/strong>eaminase <strong>a<\/strong>cting on <strong>R<\/strong>NA, oder <strong>ADAR<\/strong>), um die RNA zu modifizieren und so die Gesundheit zu erhalten. Die Gr\u00fcnder von AIRNA waren Pioniere mit der Idee, ADAR gezielt dazu zu verwenden, um pr\u00e4zise, absichtliche Ver\u00e4nderungen an der RNA zur Behandlung von Krankheiten vorzunehmen, ohne die DNA einer Person dauerhaft zu ver\u00e4ndern. <br\/><\/p>\n<\/div>\n<\/div>\n\n<\/div>\n\n\t<\/div>\n\n\n\n<figure class=\"wp-block-image size-full desktop-only\"><img decoding=\"async\" src=\"https:\/\/airna.com\/wp-content\/uploads\/2025\/07\/AIRNA-RNA-editing-mechanism-DE.png\" alt=\"\" class=\"wp-image-4661\"\/><\/figure>\n\n\n\n<figure class=\"wp-block-image size-full mobile-only\"><img decoding=\"async\" src=\"https:\/\/airna.com\/wp-content\/uploads\/2025\/07\/AIRNA-RNA-editing-mechanism-mobile-DE.png\" alt=\"\" class=\"wp-image-4660\"\/><\/figure>\n\n\n\n<div class=\"wp-block-group is-style-offset-right is-layout-constrained wp-block-group-is-layout-constrained\">\n<p>Wir entwickeln Medikamente, die ADAR genau an eine bestimmte RNA-Position leiten, um ein Adenosin (A) pr\u00e4zise in ein Inosin (I) zu \u00e4ndern, das von der genetischen Maschinerie des K\u00f6rpers als Guanosin (G) gelesen wird. Das Ergebnis: modifizierte Funktion des resultierenden Proteins, mit dem Potenzial, die Krankheit umzukehren oder zu verhindern. <\/p>\n\n\n\n<p>Wir besch\u00e4ftigen uns mit Krankheiten, bei denen der zugrunde liegende Mechanismus gut verstanden ist, aber mit anderen Ans\u00e4tzen schwer oder unm\u00f6glich zu erreichen ist und deshalb sich gut f\u00fcr RNA-Editing eignet.<\/p>\n<\/div>\n<\/div><\/div>\n\n\t<div  class=\"section-heading  align-text-left align-content-top align wp-block-acf-section-heading\">\n\t\n\n\t\t<div class=\"acf-innerblocks-container\">\n\n<div class=\"wp-block-group is-layout-constrained wp-block-group-is-layout-constrained\">\n<div class=\"wp-block-group is-style-offset-left section-heading__heading is-layout-constrained wp-block-group-is-layout-constrained\">\n<h2 class=\"wp-block-heading eyebrow-preheading\">Die Software des Lebens neu codieren <\/h2>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<h3 class=\"wp-block-heading has-h-2-font-size\">Unser Ziel ist die Entwicklung hochwirksamer Genmedikamente mit flexibler Dosierung. <\/h3>\n<\/div>\n\n\n\n<div class=\"wp-block-group is-style-offset-right section-heading__content is-layout-constrained wp-block-group-is-layout-constrained\">\n<p>Unsere Produktkandidaten sind Oligonukleotide (kurze Nukleins\u00e4ure-Str\u00e4nge) mit propriet\u00e4ren Technologien, die f\u00fcr eine erstklassige Editing-Effizienz und langfristige Best\u00e4ndigkeit, optimale Sicherheit, patientenfreundliche Darreichungsform sowie eine geringe und seltene Dosierung, die sowohl reversibel als auch wiederholbar ist, entwickelt wurden. Wir glauben, dass Patienten und \u00c4rzte diesen Ansatz aufgrund seiner bequemen und sicheren Anwendung in Kombination mit einer starken und dauerhaften Proteinproduktion bevorzugen werden.<br\/><\/p>\n<\/div>\n<\/div>\n\n<\/div>\n\n\t<\/div>\n\n<p><strong>AIRNA wurde von den wissenschaftlichen Vorreitern im Bereich ADAR-Editing gegr\u00fcndet. Erfahren Sie mehr zu Neuigkeiten in diesem Bereich. <\/strong><\/p>\n\n<div class=\"wp-block-buttons is-content-justification-center is-layout-flex wp-container-core-buttons-is-layout-a89b3969 wp-block-buttons-is-layout-flex\">\n<div class=\"wp-block-button is-style-secondary\"><a class=\"wp-block-button__link wp-element-button\" href=\"https:\/\/airna.com\/de\/news\/#publications\">Publikationen<\/a><\/div>\n<\/div>\n\n<div style=\"height:51px\" aria-hidden=\"true\" class=\"wp-block-spacer\"><\/div>\n\n<div class=\"wp-block-cover alignfull is-light cover-cta\"><span aria-hidden=\"true\" class=\"wp-block-cover__background has-background-dim-0 has-background-dim\" style=\"background-color:#c9d8fc\"><\/span><img decoding=\"async\" width=\"2560\" height=\"1565\" class=\"wp-block-cover__image-background wp-image-4610\" alt=\"\" src=\"https:\/\/airna.com\/wp-content\/uploads\/2025\/03\/AIRNA-team-science-1-scaled.jpg\" data-object-fit=\"cover\" srcset=\"https:\/\/airna.com\/wp-content\/uploads\/2025\/03\/AIRNA-team-science-1-scaled.jpg 2560w, https:\/\/airna.com\/wp-content\/uploads\/2025\/03\/AIRNA-team-science-1-300x183.jpg 300w, https:\/\/airna.com\/wp-content\/uploads\/2025\/03\/AIRNA-team-science-1-1024x626.jpg 1024w, https:\/\/airna.com\/wp-content\/uploads\/2025\/03\/AIRNA-team-science-1-768x469.jpg 768w, https:\/\/airna.com\/wp-content\/uploads\/2025\/03\/AIRNA-team-science-1-1536x939.jpg 1536w, https:\/\/airna.com\/wp-content\/uploads\/2025\/03\/AIRNA-team-science-1-2048x1252.jpg 2048w\" sizes=\"(max-width: 2560px) 100vw, 2560px\" \/><div class=\"wp-block-cover__inner-container is-layout-constrained wp-block-cover-is-layout-constrained\">\n<div class=\"wp-block-group cover-cta-inner is-content-justification-left is-layout-constrained wp-container-core-group-is-layout-c8165dcd wp-block-group-is-layout-constrained\">\n<div class=\"wp-block-group cover-cta-inner-content is-layout-constrained wp-block-group-is-layout-constrained\">\n<h4 class=\"wp-block-heading\" style=\"text-transform:uppercase\">Partnerschaften<\/h4>\n\n\n\n<hr class=\"wp-block-separator has-alpha-channel-opacity\"\/>\n\n\n\n<p><strong>AIRNA verf\u00fcgt \u00fcber umfassendes Fachwissen im Bereich pr\u00e4ziser RNA-Editierungstherapeutika f\u00fcr eine Vielzahl genetisch adressierbarer Krankheitsziele. Wir sind an strategischen Kooperationen interessiert, um diese F\u00e4higkeiten auf therapeutische Bereiche von beiderseitigem Interesse auszuweiten.<br\/><\/strong><\/p>\n\n\n\n<p class=\"link-block\"><strong>Kontakt<\/strong><br\/><a href=\"mailto:partnership@airna.com\" target=\"_blank\" rel=\"noreferrer noopener\">partnership@airna.com<\/a><\/p>\n<\/div>\n<\/div>\n<\/div><\/div>\n","protected":false},"excerpt":{"rendered":"<p>AIRNA wurde von den wissenschaftlichen Vorreitern im Bereich ADAR-Editing gegr\u00fcndet. Erfahren Sie mehr zu Neuigkeiten in diesem Bereich.<\/p>\n","protected":false},"author":1,"featured_media":0,"parent":0,"menu_order":0,"comment_status":"closed","ping_status":"closed","template":"","meta":{"_acf_changed":false,"footnotes":""},"class_list":["post-4980","page","type-page","status-publish","hentry"],"acf":[],"yoast_head":"<!-- This site is optimized with the Yoast SEO plugin v27.2 - https:\/\/yoast.com\/product\/yoast-seo-wordpress\/ -->\n<title>Wissenschaft und Plattform &#8212; Airna<\/title>\n<meta name=\"description\" content=\"Neue Erkenntnisse zu Genmedikamenten umsetzen Wir steuern ein nat\u00fcrlich vorkommendes menschliches Protein pr\u00e4zise um, so dass es therapeutischen Nutzen\" \/>\n<meta name=\"robots\" content=\"index, follow, max-snippet:-1, max-image-preview:large, max-video-preview:-1\" \/>\n<link rel=\"canonical\" href=\"https:\/\/airna.com\/de\/science-platform\/\" \/>\n<meta property=\"og:locale\" content=\"de_DE\" \/>\n<meta property=\"og:type\" content=\"article\" \/>\n<meta property=\"og:title\" content=\"Wissenschaft und Plattform &#8212; 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