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Pressemitteilungen
In den Nachrichten
Publikationen
Publications
Optimized RESTORE+ oligonucleotides for an efficacious and safe RNA base editing treatment for Alpha-1 Antitrypsin Deficiency
Publications
Precision RNA base editing with engineered and endogenous effectors
Publications
Precise RNA editing by recruiting endogenous ADARs with antisense oligonucleotides
Publications
Harnessing human ADAR2 for RNA repair – Recoding a PINK1 mutation rescues mitophagy
Publications